Orfadin Oral Suspension (Nitisinone)

Complete patient guide for uses, dosage, side effects, and safety information

Prescription Required

Quick Facts

Generic Name
nitisinone
Drug Class
other alimentary and metabolism products
Used For
treatment of hereditary tyrosinaemia type 1 (HT-1)
How Taken
oral suspension taken with an oral syringe, dosage varies

What Is Orfadin Oral Suspension Used For?

Orfadin Oral Suspension is a medication that contains nitisinone, which is used to treat hereditary tyrosinaemia type 1 (HT-1). This condition prevents the body from fully breaking down the amino acid tyrosine, leading to harmful substances accumulating in the body.

Primary Uses

Orfadin is primarily used for managing hereditary tyrosinaemia type 1 (HT-1).

How It Works

Nitisinone works by blocking the breakdown of tyrosine, preventing the formation of harmful substances.

Good to know: Orfadin is not addictive.

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How to Take Orfadin Oral Suspension

Orfadin Oral Suspension should be taken as directed by your doctor, using an oral syringe for accurate dosing.

Dosage Instructions

The recommended starting dose is 1 mg/kg body weight per day, divided into two doses. Your doctor may adjust the dosage based on your response and test results.

What If You Miss a Dose?

If you miss a dose, do not take a double dose to make up for it. Contact your doctor or pharmacist for advice.

Important: Never double dose to compensate for a missed dose.

Side Effects

Like all medications, this medicine can cause side effects. Most are mild and temporary, but some require medical attention.

Common Side Effects

These side effects occur relatively frequently and usually don’t require emergency care:

  • rash
  • itching or irritation of the skin
  • redness and peeling of skin
  • headaches
  • stomach pain
  • constipation

Seek immediate medical attention if you experience:

  • red eyes
  • scarring or clouding of the cornea
  • inflammation in the cornea
  • inflammation in the eye
  • inflammation in the eyelids
  • sensitivity to light
  • eye pain
  • shortness of breath
  • wheezing or difficulty breathing
  • swelling of the face, lips, tongue or other parts of the body

Important Warnings

There are important considerations to keep in mind while using Orfadin.

Who Should Not Take Orfadin Oral Suspension

Do not use Orfadin if you have had an allergic reaction to nitisinone or any of its ingredients.

Medical Conditions to Discuss

Inform your doctor about any other medical conditions you have or other medications you are taking.

Pregnancy and Breastfeeding

Consult your doctor if you are pregnant, plan to become pregnant, or are breastfeeding. Do not breastfeed while taking Orfadin.

Drug Interactions

Some medications may interact with Orfadin and affect its efficacy.

  • warfarin
  • phenytoin
  • furosemide (frusemide)

Alcohol & Driving

Be cautious when driving or operating machinery until you know how Orfadin affects you.

Alcohol

Consult your doctor regarding alcohol consumption while taking Orfadin.

Driving and Operating Machinery

Orfadin is not known to cause dizziness, but it may affect vision if side effects occur.

Storage

Store the unopened bottle of Orfadin in its box in a refrigerator between 2°C – 8°C. After opening, keep it in a cool place below 25°C and discard it 2 months after opening.

Overdose Information

If you suspect an overdose, seek immediate medical attention. Contact the Poisons Information Centre at 13 11 26 or go to the nearest hospital.

Frequently Asked Questions

The time it takes for Orfadin to work can vary based on individual response and treatment adherence.

Yes, Orfadin should be taken with food.

No, Orfadin is not considered addictive.

Do not stop taking Orfadin suddenly without consulting your doctor, as it may worsen your condition.

Consult your doctor regarding alcohol consumption while on Orfadin.

Weight gain is not listed as a common side effect of Orfadin.

Elderly patients should consult their doctor to ensure safety while taking Orfadin.

If you miss a dose, do not take a double dose. Contact your doctor or pharmacist for advice.

Important Disclaimer

This information is intended for general educational purposes only and should not be considered medical advice. Always consult your healthcare provider or pharmacist before starting, stopping, or changing any medication.

If you think you may have a medical emergency, call your doctor or emergency services immediately.

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