Orfadin capsules (Nitisinone)

Complete patient guide for uses, dosage, side effects, and safety information

Prescription Required

Quick Facts

Generic Name
nitisinone
Drug Class
other alimentary and metabolism products
Used For
treatment of hereditary tyrosinaemia type 1 (HT-1)
How Taken
oral capsule, typically twice daily

What Is Orfadin capsules Used For?

Orfadin capsules contain nitisinone, which is used to manage hereditary tyrosinaemia type 1 (HT-1), a condition where the body cannot fully break down the amino acid tyrosine.

Primary Uses

Orfadin is primarily used for treating hereditary tyrosinaemia type 1 (HT-1).

How It Works

Nitisinone works by blocking the breakdown of tyrosine, preventing the accumulation of harmful substances in the body.

Good to know: Orfadin is not addictive.

Continue Reading

Sign in to access the complete medication guide including dosage, side effects, warnings, and more.

How to Take Orfadin capsules

It is important to take Orfadin capsules as directed by your healthcare provider.

Dosage Instructions

The recommended starting dose is 1 mg/kg of body weight per day, divided into two doses. Your doctor may adjust this based on your response and test results.

What If You Miss a Dose?

If you miss a dose, do not take a double dose to make up for it. Consult your doctor or pharmacist for guidance.

Important: Never double your dose to compensate for a missed dose.

Available Tablet Strengths

2mg
2mg Tablet White, Hard gelatin • NTBC 2 mg
5mg
5mg Tablet White, Hard gelatin • NTBC 5 mg
10mg
10mg Tablet White, Hard gelatin • NTBC 10 mg
20mg
20mg Tablet White, Hard gelatin • NTBC 20 mg

Side Effects

Like all medications, this medicine can cause side effects. Most are mild and temporary, but some require medical attention.

Common Side Effects

These side effects occur relatively frequently and usually don’t require emergency care:

  • rash
  • itching or irritation of the skin
  • redness and peeling of skin
  • headaches
  • stomach pain
  • constipation

Seek immediate medical attention if you experience:

  • red eyes
  • scarring or clouding of the cornea
  • inflammation in the cornea
  • inflammation in the eye
  • inflammation in the eyelids
  • sensitivity to light
  • eye pain
  • shortness of breath
  • wheezing or difficulty breathing
  • swelling of the face, lips, tongue or other parts of the body

Important Warnings

There are several important considerations when using Orfadin.

Who Should Not Take Orfadin capsules

Do not use Orfadin if you have a known allergy to nitisinone or any of its ingredients.

Medical Conditions to Discuss

Inform your doctor about any other medical conditions you have or medications you are taking.

Pregnancy and Breastfeeding

Consult your doctor if you are pregnant, planning to become pregnant, or breastfeeding, as Orfadin should not be used during breastfeeding.

Drug Interactions

Certain medications may interact with Orfadin.

  • warfarin
  • phenytoin
  • furosemide (frusemide)

Alcohol & Driving

Be cautious when driving or operating machinery until you know how Orfadin affects you.

Alcohol

No specific alcohol warnings were mentioned, but consult your doctor for personalized advice.

Driving and Operating Machinery

Orfadin is not known to cause dizziness or lightheadedness, but it may affect vision if side effects occur.

Storage

Store Orfadin capsules in their original container in a refrigerator between 2°C and 8°C. They can also be kept in a cool, dry place below 25°C for up to 2 months.

Overdose Information

If you suspect an overdose of Orfadin, seek immediate medical attention. Contact your doctor or the Poisons Information Centre at 13 11 26.

Frequently Asked Questions

Orfadin helps control your condition but does not cure it. The time to notice effects may vary.

Yes, Orfadin should be taken with food.

No, Orfadin is not addictive.

Do not stop taking Orfadin without consulting your doctor, as your condition may worsen.

Consult your doctor for personalized advice regarding alcohol consumption while on Orfadin.

Weight gain is not mentioned as a side effect of Orfadin.

Consult your doctor to determine if Orfadin is safe for elderly patients.

If you miss a dose, do not take a double dose. Consult your doctor or pharmacist for guidance.

Important Disclaimer

This information is intended for general educational purposes only and should not be considered medical advice. Always consult your healthcare provider or pharmacist before starting, stopping, or changing any medication.

If you think you may have a medical emergency, call your doctor or emergency services immediately.

Create a free account to access the full medication guide.

Sign in to access your medication guides.